The administration of antisense oligonucleotide golodirsen reduces pathological regeneration in pati...
The administration of antisense oligonucleotide golodirsen reduces pathological regeneration in patients with Duchenne muscular dystrophy
About this item
Full title
Author / Creator
Scaglioni, Dominic , Catapano, Francesco , Ellis, Matthew , Torelli, Silvia , Chambers, Darren , Feng, Lucy , Beck, Matthew , Sewry, Caroline , Monforte, Mauro , Harriman, Shawn , Koenig, Erica , Malhotra, Jyoti , Popplewell, Linda , Guglieri, Michela , Straub, Volker , Mercuri, Eugenio , Servais, Laurent , Phadke, Rahul , Morgan, Jennifer and Muntoni, Francesco
Publisher
England: BioMed Central
Journal title
Language
English
Formats
Publication information
Publisher
England: BioMed Central
Subjects
More information
Scope and Contents
Contents
During the last decade, multiple clinical trials for Duchenne muscular dystrophy (DMD) have focused on the induction of dystrophin expression using different strategies. Many of these trials have reported a clear increase in dystrophin protein following treatment. However, the low levels of the induced dystrophin protein have raised questions on it...
Alternative Titles
Full title
The administration of antisense oligonucleotide golodirsen reduces pathological regeneration in patients with Duchenne muscular dystrophy
Authors, Artists and Contributors
Author / Creator
Catapano, Francesco
Ellis, Matthew
Torelli, Silvia
Chambers, Darren
Feng, Lucy
Beck, Matthew
Sewry, Caroline
Monforte, Mauro
Harriman, Shawn
Koenig, Erica
Malhotra, Jyoti
Popplewell, Linda
Guglieri, Michela
Straub, Volker
Mercuri, Eugenio
Servais, Laurent
Phadke, Rahul
Morgan, Jennifer
Muntoni, Francesco
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_doaj_primary_oai_doaj_org_article_0bb99a8919a34521a7b32c5a0a245087
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_0bb99a8919a34521a7b32c5a0a245087
Other Identifiers
ISSN
2051-5960
E-ISSN
2051-5960
DOI
10.1186/s40478-020-01106-1
