A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID
About this item
Full title
Author / Creator
Cesana, Daniela , Cicalese, Maria Pia , Calabria, Andrea , Merli, Pietro , Caruso, Roberta , Volpin, Monica , Rudilosso, Laura , Migliavacca, Maddalena , Barzaghi, Federica , Fossati, Claudia , Gazzo, Francesco , Pizzi, Simone , Ciolfi, Andrea , Bruselles, Alessandro , Tucci, Francesca , Spinozzi, Giulio , Pais, Giulia , Benedicenti, Fabrizio , Barcella, Matteo , Merelli, Ivan , Gallina, Pierangela , Giannelli, Stefania , Dionisio, Francesca , Scala, Serena , Casiraghi, Miriam , Strocchio, Luisa , Vinti, Luciana , Pacillo, Lucia , Draghi, Eleonora , Cesana, Marcella , Riccardo, Sara , Colantuono, Chiara , Six, Emmanuelle , Cavazzana, Marina , Carlucci, Filippo , Schmidt, Manfred , Cancrini, Caterina , Ciceri, Fabio , Vago, Luca , Cacchiarelli, Davide , Gentner, Bernhard , Naldini, Luigi , Tartaglia, Marco , Montini, Eugenio , Locatelli, Franco and Aiuti, Alessandro
Publisher
London: Nature Publishing Group UK
Journal title
Language
English
Formats
Publication information
Publisher
London: Nature Publishing Group UK
Subjects
More information
Scope and Contents
Contents
Hematopoietic stem cell gene therapy (GT) using a γ-retroviral vector (γ-RV) is an effective treatment for Severe Combined Immunodeficiency due to Adenosine Deaminase deficiency. Here, we describe a case of GT-related T-cell acute lymphoblastic leukemia (T-ALL) that developed 4.7 years after treatment. The patient underwent chemotherapy and haploid...
Alternative Titles
Full title
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID
Authors, Artists and Contributors
Author / Creator
Cicalese, Maria Pia
Calabria, Andrea
Merli, Pietro
Caruso, Roberta
Volpin, Monica
Rudilosso, Laura
Migliavacca, Maddalena
Barzaghi, Federica
Fossati, Claudia
Gazzo, Francesco
Pizzi, Simone
Ciolfi, Andrea
Bruselles, Alessandro
Tucci, Francesca
Spinozzi, Giulio
Pais, Giulia
Benedicenti, Fabrizio
Barcella, Matteo
Merelli, Ivan
Gallina, Pierangela
Giannelli, Stefania
Dionisio, Francesca
Scala, Serena
Casiraghi, Miriam
Strocchio, Luisa
Vinti, Luciana
Pacillo, Lucia
Draghi, Eleonora
Cesana, Marcella
Riccardo, Sara
Colantuono, Chiara
Six, Emmanuelle
Cavazzana, Marina
Carlucci, Filippo
Schmidt, Manfred
Cancrini, Caterina
Ciceri, Fabio
Vago, Luca
Cacchiarelli, Davide
Gentner, Bernhard
Naldini, Luigi
Tartaglia, Marco
Montini, Eugenio
Locatelli, Franco
Aiuti, Alessandro
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_doaj_primary_oai_doaj_org_article_319bd86d084c40b6be16ee73e0b5af1a
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_319bd86d084c40b6be16ee73e0b5af1a
Other Identifiers
ISSN
2041-1723
E-ISSN
2041-1723
DOI
10.1038/s41467-024-47866-5
