CRISPR-Based Tools for Fighting Rare Diseases
CRISPR-Based Tools for Fighting Rare Diseases
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Publisher
Switzerland: MDPI AG
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Language
English
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Publisher
Switzerland: MDPI AG
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Scope and Contents
Contents
Rare diseases affect the life of a tremendous number of people globally. The CRISPR-Cas system emerged as a powerful genome engineering tool and has facilitated the comprehension of the mechanism and development of therapies for rare diseases. This review focuses on current efforts to develop the CRISPR-based toolbox for various rare disease therap...
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Full title
CRISPR-Based Tools for Fighting Rare Diseases
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TN_cdi_doaj_primary_oai_doaj_org_article_484078d8b40745518f4bb9eb9f1768b6
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_484078d8b40745518f4bb9eb9f1768b6
Other Identifiers
ISSN
2075-1729
E-ISSN
2075-1729
DOI
10.3390/life12121968