Different solubilizing ability of cyclodextrin derivatives for cholesterol in Niemann–Pick disease t...
Different solubilizing ability of cyclodextrin derivatives for cholesterol in Niemann–Pick disease type C treatment
About this item
Full title
Author / Creator
Yamada, Yusei , Fukaura‐Nishizawa, Madoka , Nishiyama, Asami , Ishii, Akira , Kawata, Tatsuya , Shirakawa, Aina , Tanaka, Mayuko , Kondo, Yuki , Takeo, Toru , Nakagata, Naomi , Miwa, Toru , Takeda, Hiroki , Orita, Yorihisa , Motoyama, Keiichi , Higashi, Taishi , Arima, Hidetoshi , Seki, Takahiro , Kurauchi, Yuki , Katsuki, Hiroshi , Higaki, Katsumi , Minami, Kentaro , Yoshikawa, Naoki , Ikeda, Ryuji , Matsuo, Muneaki , Irie, Tetsumi and Ishitsuka, Yoichi
Publisher
Heidelberg: John Wiley & Sons, Inc
Journal title
Language
English
Formats
Publication information
Publisher
Heidelberg: John Wiley & Sons, Inc
Subjects
More information
Scope and Contents
Contents
Background
Niemann–Pick disease type C (NPC) is a fatal neurodegenerative disorder caused by abnormal intracellular cholesterol trafficking. Cyclodextrins (CDs), the most promising therapeutic candidates for NPC, but with concerns about ototoxicity, are cyclic oligosaccharides with dual functions of unesterified cholesterol (UC) shuttle and sink...
Alternative Titles
Full title
Different solubilizing ability of cyclodextrin derivatives for cholesterol in Niemann–Pick disease type C treatment
Authors, Artists and Contributors
Author / Creator
Fukaura‐Nishizawa, Madoka
Nishiyama, Asami
Ishii, Akira
Kawata, Tatsuya
Shirakawa, Aina
Tanaka, Mayuko
Kondo, Yuki
Takeo, Toru
Nakagata, Naomi
Miwa, Toru
Takeda, Hiroki
Orita, Yorihisa
Motoyama, Keiichi
Higashi, Taishi
Arima, Hidetoshi
Seki, Takahiro
Kurauchi, Yuki
Katsuki, Hiroshi
Higaki, Katsumi
Minami, Kentaro
Yoshikawa, Naoki
Ikeda, Ryuji
Matsuo, Muneaki
Irie, Tetsumi
Ishitsuka, Yoichi
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_doaj_primary_oai_doaj_org_article_4e90738b28c44e4c9ddaf53a1c5805b3
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_4e90738b28c44e4c9ddaf53a1c5805b3
Other Identifiers
ISSN
2001-1326
E-ISSN
2001-1326
DOI
10.1002/ctm2.1350