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Motor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-anal...

Motor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-anal...

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_7052ee4c081f4655ba5496e0f865c713

Motor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-analysis

About this item

Full title

Motor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-analysis

Publisher

London: BioMed Central Ltd

Journal title

Orphanet journal of rare diseases, 2021-10, Vol.16 (1), p.1-430, Article 430

Language

English

Formats

Publication information

Publisher

London: BioMed Central Ltd

More information

Scope and Contents

Contents

There is an increasing number of papers reporting the real world use of Nusinersen in different cohorts of SMA patients. Our review suggests that Nusinersen provides a favorable benefit in motor function across a wide range of SMA type 2 and 3 patients over a 10-14 month observation period. Although a direct comparison with studies reporting data f...

Alternative Titles

Full title

Motor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-analysis

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_doaj_primary_oai_doaj_org_article_7052ee4c081f4655ba5496e0f865c713

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_7052ee4c081f4655ba5496e0f865c713

Other Identifiers

ISSN

1750-1172

E-ISSN

1750-1172

DOI

10.1186/s13023-021-02065-z

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