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Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_8f349d5035a04bc69de3c05ac43b2ab3

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

About this item

Full title

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

Publisher

Switzerland: MDPI AG

Journal title

Children (Basel), 2024-05, Vol.11 (5), p.590

Language

English

Formats

Publication information

Publisher

Switzerland: MDPI AG

More information

Scope and Contents

Contents

Onasemnogene abeparvovec (OA) is the approved intravenous gene therapy for the treatment of spinal muscular atrophy (SMA). A functional copy of the human SMN1 gene was inserted into the target motor neuron cells via a viral vector, AAV9. In clinical trials, OA was infused through a peripheral venous catheter, and no data are available on central ca...

Alternative Titles

Full title

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_doaj_primary_oai_doaj_org_article_8f349d5035a04bc69de3c05ac43b2ab3

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_8f349d5035a04bc69de3c05ac43b2ab3

Other Identifiers

ISSN

2227-9067

E-ISSN

2227-9067

DOI

10.3390/children11050590

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