Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report
Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report
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Switzerland: MDPI AG
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Language
English
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Switzerland: MDPI AG
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Onasemnogene abeparvovec (OA) is the approved intravenous gene therapy for the treatment of spinal muscular atrophy (SMA). A functional copy of the human SMN1 gene was inserted into the target motor neuron cells via a viral vector, AAV9. In clinical trials, OA was infused through a peripheral venous catheter, and no data are available on central ca...
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Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report
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TN_cdi_doaj_primary_oai_doaj_org_article_8f349d5035a04bc69de3c05ac43b2ab3
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https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_8f349d5035a04bc69de3c05ac43b2ab3
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ISSN
2227-9067
E-ISSN
2227-9067
DOI
10.3390/children11050590