An open-label pilot study of recombinant granulocyte-colony stimulating factor in Friedreich’s ataxi...
An open-label pilot study of recombinant granulocyte-colony stimulating factor in Friedreich’s ataxia
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London: Nature Publishing Group UK
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Language
English
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Publisher
London: Nature Publishing Group UK
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Friedreich’s ataxia (FA) is an inherited progressive neurodegenerative disease for which there is no proven disease-modifying treatment. Here we perform an open‐label, pilot study of recombinant human granulocyte-colony stimulating factor (G-CSF) administration in seven people with FA (EudraCT: 2017-003084-34); each participant receiving a single c...
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An open-label pilot study of recombinant granulocyte-colony stimulating factor in Friedreich’s ataxia
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TN_cdi_doaj_primary_oai_doaj_org_article_cb7e58544e044c609b7610d1857a7b4a
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https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_cb7e58544e044c609b7610d1857a7b4a
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ISSN
2041-1723
E-ISSN
2041-1723
DOI
10.1038/s41467-022-31450-w
