Potential for cellular stress response to hepatic factor VIII expression from AAV vector
Potential for cellular stress response to hepatic factor VIII expression from AAV vector
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Publisher
United States: Elsevier Limited
Journal title
Language
English
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Publisher
United States: Elsevier Limited
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Scope and Contents
Contents
Hemophilia A and B are coagulation disorders resulting from the loss of functional coagulation factor VIII (FVIII) or factor IX proteins, respectively. Gene therapy for hemophilia with adeno-associated virus vectors has shown efficacy in hemophilia B patients. Although hemophilia A patients are more prevalent, the development of therapeutic adeno-a...
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Full title
Potential for cellular stress response to hepatic factor VIII expression from AAV vector
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TN_cdi_doaj_primary_oai_doaj_org_article_cc6eb2caf37342bfa894aa969350dfa7
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_cc6eb2caf37342bfa894aa969350dfa7
Other Identifiers
ISSN
2329-0501
E-ISSN
2329-0501
DOI
10.1038/mtm.2016.63
