Long-term efficacy of lipoprotein apheresis and lomitapide in the treatment of homozygous familial h...
Long-term efficacy of lipoprotein apheresis and lomitapide in the treatment of homozygous familial hypercholesterolemia (HoFH): a cross-national retrospective survey
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Author / Creator
D’Erasmo, Laura , Gallo, Antonio , Cefalù, Angelo Baldassare , Di Costanzo, Alessia , Saheb, Samir , Giammanco, Antonina , Averna, Maurizio , Buonaiuto, Alessio , Iannuzzo, Gabriella , Fortunato, Giuliana , Puja, Arturo , Montalcini, Tiziana , Pavanello, Chiara , Calabresi, Laura , Vigna, Giovanni Battista , Bucci, Marco , Bonomo, Katia , Nota, Fabio , Sampietro, Tiziana , Sbrana, Francesco , Suppressa, Patrizia , Sabbà, Carlo , Fimiani, Fabio , Cesaro, Arturo , Calabrò, Paolo , Palmisano, Silvia , D’Addato, Sergio , Pisciotta, Livia , Bertolini, Stefano , Bittar, Randa , Kalmykova, Olga , Béliard, Sophie , Carrié, Alain , Arca, Marcello and Bruckert, Eric
Publisher
London: BioMed Central Ltd
Journal title
Language
English
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Publication information
Publisher
London: BioMed Central Ltd
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More information
Scope and Contents
Contents
Homozygous familial hypercholesterolemia (HoFH) is a rare life-threatening condition that represents a therapeutic challenge. The vast majority of HoFH patients fail to achieve LDL-C targets when treated with the standard protocol, which associates maximally tolerated dose of lipid-lowering medications with lipoprotein apheresis (LA). Lomitapide is...
Alternative Titles
Full title
Long-term efficacy of lipoprotein apheresis and lomitapide in the treatment of homozygous familial hypercholesterolemia (HoFH): a cross-national retrospective survey
Authors, Artists and Contributors
Author / Creator
Gallo, Antonio
Cefalù, Angelo Baldassare
Di Costanzo, Alessia
Saheb, Samir
Giammanco, Antonina
Averna, Maurizio
Buonaiuto, Alessio
Iannuzzo, Gabriella
Fortunato, Giuliana
Puja, Arturo
Montalcini, Tiziana
Pavanello, Chiara
Calabresi, Laura
Vigna, Giovanni Battista
Bucci, Marco
Bonomo, Katia
Nota, Fabio
Sampietro, Tiziana
Sbrana, Francesco
Suppressa, Patrizia
Sabbà, Carlo
Fimiani, Fabio
Cesaro, Arturo
Calabrò, Paolo
Palmisano, Silvia
D’Addato, Sergio
Pisciotta, Livia
Bertolini, Stefano
Bittar, Randa
Kalmykova, Olga
Béliard, Sophie
Carrié, Alain
Arca, Marcello
Bruckert, Eric
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_doaj_primary_oai_doaj_org_article_d3d61cde509e4a539ecfd7328d4ab9a4
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_doaj_primary_oai_doaj_org_article_d3d61cde509e4a539ecfd7328d4ab9a4
Other Identifiers
ISSN
1750-1172
E-ISSN
1750-1172
DOI
10.1186/s13023-021-01999-8