6 Minute Walk Test in Duchenne MD Patients with Different Mutations: 12 Month Changes
6 Minute Walk Test in Duchenne MD Patients with Different Mutations: 12 Month Changes
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Author / Creator
Pane, Marika , Mazzone, Elena S. , Sormani, Maria Pia , Messina, Sonia , Vita, Gian Luca , Fanelli, Lavinia , Berardinelli, Angela , Torrente, Yvan , D'Amico, Adele , Lanzillotta, Valentina , Viggiano, Emanuela , D'Ambrosio, Paola , Cavallaro, Filippo , Frosini, Silvia , Bello, Luca , Bonfiglio, Serena , Scalise, Roberta , De Sanctis, Roberto , Rolle, Enrica , Bianco, Flaviana , Van der Haawue, Marlene , Magri, Francesca , Palermo, Concetta , Rossi, Francesca , Donati, Maria Alice , Alfonsi, Chiara , Sacchini, Michele , Arnoldi, Maria Teresa , Baranello, Giovanni , Mongini, Tiziana , Pini, Antonella , Battini, Roberta , Pegoraro, Elena , Previtali, Stefano C. , Napolitano, Sara , Bruno, Claudio , Politano, Luisa , Comi, Giacomo P. , Bertini, Enrico , Morandi, Lucia , Gualandi, Francesca , Ferlini, Alessandra , Goemans, Nathalie and Mercuri, Eugenio
Publisher
United States: Public Library of Science
Journal title
Language
English
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Publication information
Publisher
United States: Public Library of Science
Subjects
More information
Scope and Contents
Contents
In the last few years some of the therapeutical approaches for Duchenne muscular dystrophy (DMD) are specifically targeting distinct groups of mutations, such as deletions eligible for skipping of individual exons. The aim of this observational study was to establish whether patients with distinct groups of mutations have different profiles of chan...
Alternative Titles
Full title
6 Minute Walk Test in Duchenne MD Patients with Different Mutations: 12 Month Changes
Authors, Artists and Contributors
Author / Creator
Mazzone, Elena S.
Sormani, Maria Pia
Messina, Sonia
Vita, Gian Luca
Fanelli, Lavinia
Berardinelli, Angela
Torrente, Yvan
D'Amico, Adele
Lanzillotta, Valentina
Viggiano, Emanuela
D'Ambrosio, Paola
Cavallaro, Filippo
Frosini, Silvia
Bello, Luca
Bonfiglio, Serena
Scalise, Roberta
De Sanctis, Roberto
Rolle, Enrica
Bianco, Flaviana
Van der Haawue, Marlene
Magri, Francesca
Palermo, Concetta
Rossi, Francesca
Donati, Maria Alice
Alfonsi, Chiara
Sacchini, Michele
Arnoldi, Maria Teresa
Baranello, Giovanni
Mongini, Tiziana
Pini, Antonella
Battini, Roberta
Pegoraro, Elena
Previtali, Stefano C.
Napolitano, Sara
Bruno, Claudio
Politano, Luisa
Comi, Giacomo P.
Bertini, Enrico
Morandi, Lucia
Gualandi, Francesca
Ferlini, Alessandra
Goemans, Nathalie
Mercuri, Eugenio
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Primary Identifiers
Record Identifier
TN_cdi_plos_journals_1476178037
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_plos_journals_1476178037
Other Identifiers
ISSN
1932-6203
E-ISSN
1932-6203
DOI
10.1371/journal.pone.0083400