P1 Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progr...
P1 Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED database
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Author / Creator
Hansen, Bettina , Valcheva, Velichka , Yu, Qifeng , Daan BE van Wessel , Thompson, Richard J , Gonzales, Emmanuel , Jankowska, Irena , Sokal, Etienne , Grammatikopoulos, Tassos , Kadaristiana, Agustina , Jacquemin, Emmanuel , Spraul, Anne , Lipiński, Patryk , Czubkowski, Piotr , Rock, Nathalie , Shagrani, Mohammad , Kumar, Kishwer , Alkuraya, Fowzan , Meddirevula Sateesh , Broering, Dieter , Nicastro, Emanuele , Kelly, Deirdre A , Nebbia, Gabriella , Arnell, Henrik , Fischler, Björn , Serranti, Daniele , Arikan, Cigdem , Polat, Esra , Debray, Dominique , Lacaille, Florence , Goncalves, Cristina , Hierro, Loreto , Gema Muñoz Bartolo , Mozer-Glassberg, Yael , Azaz, Amer , Brecelj, Jernej , Antal Dezsőfi , Calvo, Pier Luigi , Enke Grabhorn , Sturm, Ekkehard , Wendy L van der Woerd , Kamath, Binita M , Wang, Jian-She , Li, Liting , Durmaz, Özlem , Onal, Zerrin , Felzen, Antonia , Nomden, Mark , Sonajalg, Jaak , Stein, Philip , Ni, Quanhong , Clemson, Christine , Mattsson, Jan P and Verkade, Henkjan J
Publisher
London: BMJ Publishing Group LTD
Journal title
Language
English
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Publication information
Publisher
London: BMJ Publishing Group LTD
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More information
Scope and Contents
Contents
BackgroundProgressive familial intrahepatic cholestasis (PFIC) is a group of rare cholestatic liver diseases characterised by intractable pruritus, elevated serum bile acids (sBAs), and progressive liver damage. NAPPED (NAtural course and Prognosis of PFIC and Effect of biliary Diversion) is a large retrospective database investigating the natural...
Alternative Titles
Full title
P1 Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED database
Authors, Artists and Contributors
Author / Creator
Valcheva, Velichka
Yu, Qifeng
Daan BE van Wessel
Thompson, Richard J
Gonzales, Emmanuel
Jankowska, Irena
Sokal, Etienne
Grammatikopoulos, Tassos
Kadaristiana, Agustina
Jacquemin, Emmanuel
Spraul, Anne
Lipiński, Patryk
Czubkowski, Piotr
Rock, Nathalie
Shagrani, Mohammad
Kumar, Kishwer
Alkuraya, Fowzan
Meddirevula Sateesh
Broering, Dieter
Nicastro, Emanuele
Kelly, Deirdre A
Nebbia, Gabriella
Arnell, Henrik
Fischler, Björn
Serranti, Daniele
Arikan, Cigdem
Polat, Esra
Debray, Dominique
Lacaille, Florence
Goncalves, Cristina
Hierro, Loreto
Gema Muñoz Bartolo
Mozer-Glassberg, Yael
Azaz, Amer
Brecelj, Jernej
Antal Dezsőfi
Calvo, Pier Luigi
Enke Grabhorn
Sturm, Ekkehard
Wendy L van der Woerd
Kamath, Binita M
Wang, Jian-She
Li, Liting
Durmaz, Özlem
Onal, Zerrin
Felzen, Antonia
Nomden, Mark
Sonajalg, Jaak
Stein, Philip
Ni, Quanhong
Clemson, Christine
Mattsson, Jan P
Verkade, Henkjan J
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_proquest_journals_2866402552
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_journals_2866402552
Other Identifiers
ISSN
0017-5749
E-ISSN
1468-3288
DOI
10.1136/gutjnl-2023-BASL.17
