Effectiveness and Safety of Eliglustat Treatment in Gaucher Disease: Real-life Unicentric Experience
Effectiveness and Safety of Eliglustat Treatment in Gaucher Disease: Real-life Unicentric Experience
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United States: Elsevier Inc
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English
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United States: Elsevier Inc
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AbstractPurposeThe therapy and management of Gaucher disease (GD) have radically changed with the use of substrate reduction therapy, of which eliglustat is the most widely known drug, allowing it to overcome the limits of enzyme replacement therapy (ERT). The rarity of GD and the limited use of eliglustat outside clinical trials require further st...
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Effectiveness and Safety of Eliglustat Treatment in Gaucher Disease: Real-life Unicentric Experience
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TN_cdi_proquest_miscellaneous_2866379272
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https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_2866379272
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ISSN
0149-2918
E-ISSN
1879-114X
DOI
10.1016/j.clinthera.2023.08.010
