Hypophosphatasia: presentation and response to asfotase alfa
Hypophosphatasia: presentation and response to asfotase alfa
About this item
Full title
Author / Creator
Alsarraf, F. , Ali, D.S. , Almonaei, K. , Al-Alwani, H. , Khan, A.A. and Brandi, M.L.
Publisher
London: Springer London
Journal title
Language
English
Formats
Publication information
Publisher
London: Springer London
Subjects
More information
Scope and Contents
Contents
Summary
Hypophosphatasia (HPP) is a rare bone disease with limited scientific evidence on the tolerability and safety of its novel treatment, Asfotase Alfa (AA). We report 7 HPP patients’ heterogenous presentations and the significant improvement in various clinical outcomes attained with AA shedding light on this highly effective and safe thera...
Alternative Titles
Full title
Hypophosphatasia: presentation and response to asfotase alfa
Authors, Artists and Contributors
Author / Creator
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_proquest_miscellaneous_2892946555
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_2892946555
Other Identifiers
ISSN
0937-941X
E-ISSN
1433-2965
DOI
10.1007/s00198-023-06943-z
