Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia
Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia
About this item
Full title
Author / Creator
Locatelli, Franco , Lang, Peter , Wall, Donna , Meisel, Roland , Corbacioglu, Selim , Li, Amanda M. , de la Fuente, Josu , Shah, Ami J. , Carpenter, Ben , Kwiatkowski, Janet L. , Mapara, Markus , Liem, Robert I. , Cappellini, Maria Domenica , Algeri, Mattia , Kattamis, Antonis , Sheth, Sujit , Grupp, Stephan , Handgretinger, Rupert , Kohli, Puja , Shi, Daoyuan , Ross, Leorah , Bobruff, Yael , Simard, Christopher , Zhang, Lanju , Morrow, Phuong Khanh , Hobbs, William E. , Frangoul, Haydar and CLIMB THAL-111 Study Group
Publisher
United States: Massachusetts Medical Society
Journal title
Language
English
Formats
Publication information
Publisher
United States: Massachusetts Medical Society
Subjects
More information
Scope and Contents
Contents
Of 35 patients with transfusion-dependent β-thalassemia treated with gene-edited autologous hematopoietic stem and progenitor cells, 32 had hemoglobin levels maintained without red-cell transfusions for at least 12 consecutive months.
Alternative Titles
Full title
Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia
Authors, Artists and Contributors
Author / Creator
Lang, Peter
Wall, Donna
Meisel, Roland
Corbacioglu, Selim
Li, Amanda M.
de la Fuente, Josu
Shah, Ami J.
Carpenter, Ben
Kwiatkowski, Janet L.
Mapara, Markus
Liem, Robert I.
Cappellini, Maria Domenica
Algeri, Mattia
Kattamis, Antonis
Sheth, Sujit
Grupp, Stephan
Handgretinger, Rupert
Kohli, Puja
Shi, Daoyuan
Ross, Leorah
Bobruff, Yael
Simard, Christopher
Zhang, Lanju
Morrow, Phuong Khanh
Hobbs, William E.
Frangoul, Haydar
CLIMB THAL-111 Study Group
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_proquest_miscellaneous_3046516229
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_3046516229
Other Identifiers
ISSN
0028-4793,1533-4406
E-ISSN
1533-4406
DOI
10.1056/NEJMoa2309673
