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Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_3060374827

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

About this item

Full title

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

Journal title

Children (Basel, Switzerland), 2024, Vol.11 (5)

Language

English

Formats

More information

Scope and Contents

Contents

Onasemnogene abeparvovec (OA) is the approved intravenous gene therapy for the treatment of spinal muscular atrophy (SMA). A functional copy of the human SMN1 gene was inserted into the target motor neuron cells via a viral vector, AAV9. In clinical trials, OA was infused through a peripheral venous catheter, and no data are available on central ca...

Alternative Titles

Full title

Onasemnogene Abeparvovec Administration via Peripherally Inserted Central Catheter: A Case Report

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_proquest_miscellaneous_3060374827

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_3060374827

Other Identifiers

ISSN

2227-9067

E-ISSN

2227-9067

DOI

10.3390/children11050590

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