Home treatment with enzyme replacement therapy for mucopolysaccharidosis type I is feasible and safe
Home treatment with enzyme replacement therapy for mucopolysaccharidosis type I is feasible and safe
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Publisher
Dordrecht: Dordrecht : Springer Netherlands
Journal title
Language
English
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Publisher
Dordrecht: Dordrecht : Springer Netherlands
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Scope and Contents
Contents
Objective: Intravenous enzyme replacement therapy (ERT) with recombinant α-l-iduronidase may ameliorate the non-neurological symptoms in patients with mucopolysaccharidosis type I (MPS I). Since home-based ERT for Gaucher and Fabry diseases has been reported to be safe and successful, we investigated the feasibility and safety of home therapy in pa...
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Full title
Home treatment with enzyme replacement therapy for mucopolysaccharidosis type I is feasible and safe
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TN_cdi_proquest_miscellaneous_69025885
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_69025885
Other Identifiers
ISSN
0141-8955
E-ISSN
1573-2665
DOI
10.1007/s10545-007-0686-8
