Clinically relevant therapeutic endpoints in type I Gaucher disease
Clinically relevant therapeutic endpoints in type I Gaucher disease
About this item
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Author / Creator
Publisher
Dordrecht: Kluwer Academic Publishers
Journal title
Language
English
Formats
Publication information
Publisher
Dordrecht: Kluwer Academic Publishers
Subjects
More information
Scope and Contents
Contents
The introduction of enzyme supplementation therapy for Gaucherdisease has had a great impact on the lives of many patients. Organomegaly, cytopenia and bone disease have been shown to improve in response to treatment, resulting in an improvement in quality of life. However, the assessment of organ system involvement is not always done in such a way...
Alternative Titles
Full title
Clinically relevant therapeutic endpoints in type I Gaucher disease
Authors, Artists and Contributors
Author / Creator
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Record Identifier
TN_cdi_proquest_miscellaneous_72330393
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_72330393
Other Identifiers
ISSN
0141-8955
E-ISSN
1573-2665
DOI
10.1023/A:1012492429191
