Bicalutamide and Trehalose Ameliorate Spinal and Bulbar Muscular Atrophy Pathology in Mice
Bicalutamide and Trehalose Ameliorate Spinal and Bulbar Muscular Atrophy Pathology in Mice
About this item
Full title
Author / Creator
Galbiati, Mariarita , Meroni, Marco , Boido, Marina , Cescon, Matilde , Rusmini, Paola , Crippa, Valeria , Cristofani, Riccardo , Piccolella, Margherita , Ferrari, Veronica , Tedesco, Barbara , Casarotto, Elena , Chierichetti, Marta , Cozzi, Marta , Mina, Francesco , Cicardi, Maria Elena , Pedretti, Silvia , Mitro, Nico , Caretto, Anna , Risè, Patrizia , Sala, Angelo , Lieberman, Andrew P. , Bonaldo, Paolo , Pennuto, Maria , Vercelli, Alessandro and Poletti, Angelo
Publisher
Cham: Springer International Publishing
Journal title
Language
English
Formats
Publication information
Publisher
Cham: Springer International Publishing
Subjects
More information
Scope and Contents
Contents
Spinal and bulbar muscular atrophy (SBMA) is characterized by motor neuron (MN) degeneration that leads to slowly progressive muscle weakness. It is considered a neuromuscular disease since muscle has a primary role in disease onset and progression. SBMA is caused by a CAG triplet repeat expansion in the androgen receptor (
AR
) gene. The tra...
Alternative Titles
Full title
Bicalutamide and Trehalose Ameliorate Spinal and Bulbar Muscular Atrophy Pathology in Mice
Authors, Artists and Contributors
Author / Creator
Meroni, Marco
Boido, Marina
Cescon, Matilde
Rusmini, Paola
Crippa, Valeria
Cristofani, Riccardo
Piccolella, Margherita
Ferrari, Veronica
Tedesco, Barbara
Casarotto, Elena
Chierichetti, Marta
Cozzi, Marta
Mina, Francesco
Cicardi, Maria Elena
Pedretti, Silvia
Mitro, Nico
Caretto, Anna
Risè, Patrizia
Sala, Angelo
Lieberman, Andrew P.
Bonaldo, Paolo
Pennuto, Maria
Vercelli, Alessandro
Poletti, Angelo
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_10121997
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_10121997
Other Identifiers
ISSN
1933-7213,1878-7479
E-ISSN
1878-7479
DOI
10.1007/s13311-023-01343-x