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Pomalidomide for Epistaxis in Hereditary Hemorrhagic Telangiectasia

Pomalidomide for Epistaxis in Hereditary Hemorrhagic Telangiectasia

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_11412318

Pomalidomide for Epistaxis in Hereditary Hemorrhagic Telangiectasia

About this item

Full title

Pomalidomide for Epistaxis in Hereditary Hemorrhagic Telangiectasia

Publisher

United States: Massachusetts Medical Society

Journal title

The New England journal of medicine, 2024-09, Vol.391 (11), p.1015-1027

Language

English

Formats

Publication information

Publisher

United States: Massachusetts Medical Society

More information

Scope and Contents

Contents

Hereditary hemorrhagic telangiectasia (HHT) is characterized by extensive telangiectasias and arteriovenous malformations. The primary clinical manifestation is epistaxis that results in iron-deficiency anemia and reduced health-related quality of life.
We conducted a randomized, placebo-controlled trial to evaluate the safety and efficacy of po...

Alternative Titles

Full title

Pomalidomide for Epistaxis in Hereditary Hemorrhagic Telangiectasia

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_11412318

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_11412318

Other Identifiers

ISSN

0028-4793,1533-4406

E-ISSN

1533-4406

DOI

10.1056/NEJMoa2312749

How to access this item