Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function...
Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase
About this item
Full title
Author / Creator
Harmatz, Paul , Yu, Zi-Fan , Giugliani, Roberto , Schwartz, Ida Vanessa D , Guffon, Nathalie , Teles, Elisa Leão , Miranda, M. Clara Sá , Wraith, J. Edmond , Beck, Michael , Arash, Laila , Scarpa, Maurizio , Ketteridge, David , Hopwood, John J , Plecko, Barbara , Steiner, Robert , Whitley, Chester B , Kaplan, Paige , Swiedler, Stuart J , Hardy, Karen , Berger, Kenneth I and Decker, Celeste
Publisher
Dordrecht: Dordrecht : Springer Netherlands
Journal title
Language
English
Formats
Publication information
Publisher
Dordrecht: Dordrecht : Springer Netherlands
Subjects
More information
Scope and Contents
Contents
Pulmonary function is impaired in untreated mucopolysaccharidosis type VI (MPS VI). Pulmonary function was studied in patients during long-term enzyme replacement therapy (ERT) with recombinant human arylsulfatase B (rhASB; rhN-acetylgalactosamine 4-sulfatase). Pulmonary function tests prior to and for up to 240 weeks of weekly infusions of rhASB a...
Alternative Titles
Full title
Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase
Authors, Artists and Contributors
Author / Creator
Yu, Zi-Fan
Giugliani, Roberto
Schwartz, Ida Vanessa D
Guffon, Nathalie
Teles, Elisa Leão
Miranda, M. Clara Sá
Wraith, J. Edmond
Beck, Michael
Arash, Laila
Scarpa, Maurizio
Ketteridge, David
Hopwood, John J
Plecko, Barbara
Steiner, Robert
Whitley, Chester B
Kaplan, Paige
Swiedler, Stuart J
Hardy, Karen
Berger, Kenneth I
Decker, Celeste
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_2828556
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_2828556
Other Identifiers
ISSN
0141-8955
E-ISSN
1573-2665
DOI
10.1007/s10545-009-9007-8
