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Current Status of Pharmaceutical and Genetic Therapeutic Approaches to Treat DMD

Current Status of Pharmaceutical and Genetic Therapeutic Approaches to Treat DMD

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_3098643

Current Status of Pharmaceutical and Genetic Therapeutic Approaches to Treat DMD

About this item

Full title

Current Status of Pharmaceutical and Genetic Therapeutic Approaches to Treat DMD

Publisher

United States: Elsevier Inc

Journal title

Molecular therapy, 2011-05, Vol.19 (5), p.830-840

Language

English

Formats

Publication information

Publisher

United States: Elsevier Inc

More information

Scope and Contents

Contents

Duchenne muscular dystrophy (DMD) is a genetic disease affecting about one in every 3,500 boys. This X-linked pathology is due to the absence of dystrophin in muscle fibers. This lack of dystrophin leads to the progressive muscle degeneration that is often responsible for the death of the DMD patients during the third decade of their life. There ar...

Alternative Titles

Full title

Current Status of Pharmaceutical and Genetic Therapeutic Approaches to Treat DMD

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_3098643

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_3098643

Other Identifiers

ISSN

1525-0016

E-ISSN

1525-0024

DOI

10.1038/mt.2011.59

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