Profile of eliglustat tartrate in the management of Gaucher disease
Profile of eliglustat tartrate in the management of Gaucher disease
About this item
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Author / Creator
Publisher
New Zealand: Dove Medical Press Limited
Journal title
Language
English
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Publication information
Publisher
New Zealand: Dove Medical Press Limited
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Scope and Contents
Contents
Gaucher disease (GD) is a lysosomal storage disorder caused by the deficient activity of acid beta glucosidase, with consequent accumulation of glucosylceramide in the spleen, liver, bone marrow, and various organs and tissues. Currently, the gold standard for GD treatment is enzyme replacement therapy (ERT). The efficacy of ERT in improving or sta...
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Full title
Profile of eliglustat tartrate in the management of Gaucher disease
Authors, Artists and Contributors
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Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_4714736
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_4714736
Other Identifiers
ISSN
1178-203X,1176-6336
E-ISSN
1178-203X
DOI
10.2147/TCRM.S73226
