Long-term exposure to Myozyme results in a decrease of anti-drug antibodies in late-onset Pompe dise...
Long-term exposure to Myozyme results in a decrease of anti-drug antibodies in late-onset Pompe disease patients
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Author / Creator
French Pompe Registry Study Group , Masat, Elisa , Laforêt, Pascal , De Antonio, Marie , Corre, Guillaume , Perniconi, Barbara , Taouagh, Nadjib , Mariampillai, Kuberaka , Amelin, Damien , Mauhin, Wladimir , Hogrel, Jean-Yves , Caillaud, Catherine , Ronzitti, Giuseppe , Puzzo, Francesco , Kuranda, Klaudia , Colella, Pasqualina , Mallone, Roberto , Benveniste, Olivier , Mingozzi, Federico , Bassez, G. , Bedat-Millet, A. L. , Behin, A. , Eymard, B. , Leonard-Louis, S. , Stojkovic, T. , Canal, A. , Decostre, V. , Bouhour, F. , Boyer, F. , Castaing, Y. , Chapon, F. , Cintas, P. , Durieu, I. , Echaniz-Laguna, A. , Feasson, L. , Furby, A. , Hamroun, D. , Ferrer, X. , Solé, G. , Froissart, R. , Piraud, M. , Germain, D. , Benistan, K. , Guffon-Fouilhoux, N. , Journel, H. , Labauge, P. , Lacour, A. , Levy, A. , Magot, A. , Péréon, Y. , Minot-Myhié, M. -C. , Nadaj-Pakleza, A. , Nathier, C. , Orlikowski, D. , Pellegrini, N. , Petiot, P. , Praline, J. , Lofaso, F. , Prigent, H. , Dutry, A. , Renard, D. , Sacconi, S. , Desnuelle, C. , Salort-Campana, E. , Pouget, J. , Tiffreau, V. , Vincent, D. and Zagnoli, F.
Publisher
London: Nature Publishing Group UK
Journal title
Language
English
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Publication information
Publisher
London: Nature Publishing Group UK
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More information
Scope and Contents
Contents
Immunogenicity of recombinant human acid-alpha glucosidase (rhGAA) in enzyme replacement therapy (ERT) is a safety and efficacy concern in the management of late-onset Pompe disease (LOPD). However, long-term effects of ERT on humoral and cellular responses to rhGAA are still poorly understood. To better understand the impact of immunogenicity of r...
Alternative Titles
Full title
Long-term exposure to Myozyme results in a decrease of anti-drug antibodies in late-onset Pompe disease patients
Authors, Artists and Contributors
Author / Creator
Masat, Elisa
Laforêt, Pascal
De Antonio, Marie
Corre, Guillaume
Perniconi, Barbara
Taouagh, Nadjib
Mariampillai, Kuberaka
Amelin, Damien
Mauhin, Wladimir
Hogrel, Jean-Yves
Caillaud, Catherine
Ronzitti, Giuseppe
Puzzo, Francesco
Kuranda, Klaudia
Colella, Pasqualina
Mallone, Roberto
Benveniste, Olivier
Mingozzi, Federico
Bassez, G.
Bedat-Millet, A. L.
Behin, A.
Eymard, B.
Leonard-Louis, S.
Stojkovic, T.
Canal, A.
Decostre, V.
Bouhour, F.
Boyer, F.
Castaing, Y.
Chapon, F.
Cintas, P.
Durieu, I.
Echaniz-Laguna, A.
Feasson, L.
Furby, A.
Hamroun, D.
Ferrer, X.
Solé, G.
Froissart, R.
Piraud, M.
Germain, D.
Benistan, K.
Guffon-Fouilhoux, N.
Journel, H.
Labauge, P.
Lacour, A.
Levy, A.
Magot, A.
Péréon, Y.
Minot-Myhié, M. -C.
Nadaj-Pakleza, A.
Nathier, C.
Orlikowski, D.
Pellegrini, N.
Petiot, P.
Praline, J.
Lofaso, F.
Prigent, H.
Dutry, A.
Renard, D.
Sacconi, S.
Desnuelle, C.
Salort-Campana, E.
Pouget, J.
Tiffreau, V.
Vincent, D.
Zagnoli, F.
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_5096052
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_5096052
Other Identifiers
ISSN
2045-2322
E-ISSN
2045-2322
DOI
10.1038/srep36182
