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Progress toward Gene Therapy for Duchenne Muscular Dystrophy

Progress toward Gene Therapy for Duchenne Muscular Dystrophy

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_5417844

Progress toward Gene Therapy for Duchenne Muscular Dystrophy

About this item

Full title

Progress toward Gene Therapy for Duchenne Muscular Dystrophy

Publisher

United States: Elsevier Inc

Journal title

Molecular therapy, 2017-05, Vol.25 (5), p.1125-1131

Language

English

Formats

Publication information

Publisher

United States: Elsevier Inc

More information

Scope and Contents

Contents

Duchenne muscular dystrophy (DMD) has been a major target for gene therapy development for nearly 30 years. DMD is among the most common genetic diseases, and isolation of the defective gene (DMD, or dystrophin) was a landmark discovery, as it was the first time a human disease gene had been cloned without knowledge of the protein product. Despite...

Alternative Titles

Full title

Progress toward Gene Therapy for Duchenne Muscular Dystrophy

Authors, Artists and Contributors

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_5417844

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_5417844

Other Identifiers

ISSN

1525-0016

E-ISSN

1525-0024

DOI

10.1016/j.ymthe.2017.02.019

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