Rare Opportunities: CRISPR/Cas-Based Therapy Development for Rare Genetic Diseases
Rare Opportunities: CRISPR/Cas-Based Therapy Development for Rare Genetic Diseases
About this item
Full title
Author / Creator
Publisher
Cham: Springer International Publishing
Journal title
Language
English
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Publication information
Publisher
Cham: Springer International Publishing
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Scope and Contents
Contents
Rare diseases pose a global challenge, in that their collective impact on health systems is considerable, whereas their individually rare occurrence impedes research and development of efficient therapies. In consequence, patients and their families are often unable to find an expert for their affliction, let alone a cure. The tide is turning as ph...
Alternative Titles
Full title
Rare Opportunities: CRISPR/Cas-Based Therapy Development for Rare Genetic Diseases
Authors, Artists and Contributors
Author / Creator
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Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_6469594
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_6469594
Other Identifiers
ISSN
1177-1062
E-ISSN
1179-2000
DOI
10.1007/s40291-019-00392-3
