Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integrat...
Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction
About this item
Full title
Author / Creator
Suzuki, Keiichiro , Yamamoto, Mako , Hernandez-Benitez, Reyna , Li, Zhe , Wei, Christopher , Soligalla, Rupa Devi , Aizawa, Emi , Hatanaka, Fumiyuki , Kurita, Masakazu , Reddy, Pradeep , Ocampo, Alejandro , Hishida, Tomoaki , Sakurai, Masahiro , Nemeth, Amy N. , Nuñez Delicado, Estrella , Campistol, Josep M. , Magistretti, Pierre , Guillen, Pedro , Rodriguez Esteban, Concepcion , Gong, Jianhui , Yuan, Yilin , Gu, Ying , Liu, Guang-Hui , López-Otín, Carlos , Wu, Jun , Zhang, Kun and Izpisua Belmonte, Juan Carlos
Publisher
London: Nature Publishing Group UK
Journal title
Language
English
Formats
Publication information
Publisher
London: Nature Publishing Group UK
Subjects
More information
Scope and Contents
Contents
In vivo genome editing represents a powerful strategy for both understanding basic biology and treating inherited diseases. However, it remains a challenge to develop universal and efficient in vivo genome-editing tools for tissues that comprise diverse cell types in either a dividing or non-dividing state. Here, we describe a versatile in vivo gen...
Alternative Titles
Full title
Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction
Authors, Artists and Contributors
Author / Creator
Yamamoto, Mako
Hernandez-Benitez, Reyna
Li, Zhe
Wei, Christopher
Soligalla, Rupa Devi
Aizawa, Emi
Hatanaka, Fumiyuki
Kurita, Masakazu
Reddy, Pradeep
Ocampo, Alejandro
Hishida, Tomoaki
Sakurai, Masahiro
Nemeth, Amy N.
Nuñez Delicado, Estrella
Campistol, Josep M.
Magistretti, Pierre
Guillen, Pedro
Rodriguez Esteban, Concepcion
Gong, Jianhui
Yuan, Yilin
Gu, Ying
Liu, Guang-Hui
López-Otín, Carlos
Wu, Jun
Zhang, Kun
Izpisua Belmonte, Juan Carlos
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_6796851
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_6796851
Other Identifiers
ISSN
1001-0602
E-ISSN
1748-7838
DOI
10.1038/s41422-019-0213-0