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Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integrat...

Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integrat...

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_6796851

Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction

About this item

Full title

Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction

Publisher

London: Nature Publishing Group UK

Journal title

Cell research, 2019-10, Vol.29 (10), p.804-819

Language

English

Formats

Publication information

Publisher

London: Nature Publishing Group UK

More information

Scope and Contents

Contents

In vivo genome editing represents a powerful strategy for both understanding basic biology and treating inherited diseases. However, it remains a challenge to develop universal and efficient in vivo genome-editing tools for tissues that comprise diverse cell types in either a dividing or non-dividing state. Here, we describe a versatile in vivo gen...

Alternative Titles

Full title

Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_6796851

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_6796851

Other Identifiers

ISSN

1001-0602

E-ISSN

1748-7838

DOI

10.1038/s41422-019-0213-0

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