Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in pat...
Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis
About this item
Full title
Author / Creator
González-Duarte, Alejandra , Berk, John L. , Quan, Dianna , Mauermann, Michelle L. , Schmidt, Hartmut H. , Polydefkis, Michael , Waddington-Cruz, Márcia , Ueda, Mitsuharu , Conceição, Isabel M. , Kristen, Arnt V. , Coelho, Teresa , Cauquil, Cécile A. , Tard, Céline , Merkel, Madeline , Aldinc, Emre , Chen, Jihong , Sweetser, Marianne T. , Wang, Jing Jing and Adams, David
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Journal title
Language
English
Formats
Publication information
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Subjects
More information
Scope and Contents
Contents
Hereditary transthyretin-mediated (hATTR) amyloidosis is a progressive, debilitating disease often resulting in early-onset, life-impacting autonomic dysfunction. The effect of the RNAi therapeutic, patisiran, on autonomic neuropathy manifestations in patients with hATTR amyloidosis with polyneuropathy in the phase III APOLLO study is reported. Pat...
Alternative Titles
Full title
Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis
Authors, Artists and Contributors
Author / Creator
Berk, John L.
Quan, Dianna
Mauermann, Michelle L.
Schmidt, Hartmut H.
Polydefkis, Michael
Waddington-Cruz, Márcia
Ueda, Mitsuharu
Conceição, Isabel M.
Kristen, Arnt V.
Coelho, Teresa
Cauquil, Cécile A.
Tard, Céline
Merkel, Madeline
Aldinc, Emre
Chen, Jihong
Sweetser, Marianne T.
Wang, Jing Jing
Adams, David
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7035216
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7035216
Other Identifiers
ISSN
0340-5354
E-ISSN
1432-1459
DOI
10.1007/s00415-019-09602-8
