Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis
Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis
About this item
Full title
Author / Creator
Coelho, Teresa , Yarlas, Aaron , Waddington-Cruz, Marcia , White, Michelle K. , Sikora Kessler, Asia , Lovley, Andrew , Pollock, Michael , Guthrie, Spencer , Ackermann, Elizabeth J. , Hughes, Steven G. , Karam, Chafic , Khella, Sami , Gertz, Morie , Merlini, Giampaolo , Obici, Laura , Schmidt, Hartmut H. , Polydefkis, Michael , Dyck, P. James B. , Brannagan III, Thomas H. , Conceição, Isabel , Benson, Merrill D. and Berk, John L.
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Journal title
Language
English
Formats
Publication information
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Subjects
More information
Scope and Contents
Contents
Objective
To examine the impact on quality of life (QOL) of patients with hATTR amyloidosis with polyneuropathy treated with inotersen (Tegsedi™) versus placebo.
Methods
Data were from the NEURO-TTR trial (ClinicalTrials.gov Identifier: NCT01737398), a phase 3, multinational, randomized, double-blind, placebo-controlled study of inotersen...
Alternative Titles
Full title
Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis
Authors, Artists and Contributors
Author / Creator
Yarlas, Aaron
Waddington-Cruz, Marcia
White, Michelle K.
Sikora Kessler, Asia
Lovley, Andrew
Pollock, Michael
Guthrie, Spencer
Ackermann, Elizabeth J.
Hughes, Steven G.
Karam, Chafic
Khella, Sami
Gertz, Morie
Merlini, Giampaolo
Obici, Laura
Schmidt, Hartmut H.
Polydefkis, Michael
Dyck, P. James B.
Brannagan III, Thomas H.
Conceição, Isabel
Benson, Merrill D.
Berk, John L.
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7109169
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7109169
Other Identifiers
ISSN
0340-5354
E-ISSN
1432-1459
DOI
10.1007/s00415-019-09671-9