Prednisolone rescues Duchenne muscular dystrophy phenotypes in human pluripotent stem cell–derived s...
Prednisolone rescues Duchenne muscular dystrophy phenotypes in human pluripotent stem cell–derived skeletal muscle in vitro
About this item
Full title
Author / Creator
Tanoury, Ziad Al , Zimmerman, John F. , Rao, Jyoti , Sieiro, Daniel , McNamara, Harold M. , Cherrier, Thomas , Rodríguez-delaRosa, Alejandra , Hick-Colin, Aurore , Bousson, Fanny , Fugier-Schmucker, Charlotte , Marchiano, Fabio , Habermann, Bianca , Chal, Jérome , Nesmith, Alexander P. , Gapon, Svetlana , Wagner, Erica , Gupta, Vandana A. , Bassel-Duby, Rhonda , Olson, Eric N. , Cohen, Adam E. , Parker, Kevin Kit and Pourquié, Olivier
Publisher
United States: National Academy of Sciences
Journal title
Language
English
Formats
Publication information
Publisher
United States: National Academy of Sciences
Subjects
More information
Scope and Contents
Contents
Duchenne muscular dystrophy (DMD) is a devastating genetic disease leading to degeneration of skeletal muscles and premature death. How dystrophin absence leads to muscle wasting remains unclear. Here, we describe an optimized protocol to differentiate human induced pluripotent stem cells (iPSC) to a late myogenic stage. This allows us to recapitul...
Alternative Titles
Full title
Prednisolone rescues Duchenne muscular dystrophy phenotypes in human pluripotent stem cell–derived skeletal muscle in vitro
Authors, Artists and Contributors
Author / Creator
Zimmerman, John F.
Rao, Jyoti
Sieiro, Daniel
McNamara, Harold M.
Cherrier, Thomas
Rodríguez-delaRosa, Alejandra
Hick-Colin, Aurore
Bousson, Fanny
Fugier-Schmucker, Charlotte
Marchiano, Fabio
Habermann, Bianca
Chal, Jérome
Nesmith, Alexander P.
Gapon, Svetlana
Wagner, Erica
Gupta, Vandana A.
Bassel-Duby, Rhonda
Olson, Eric N.
Cohen, Adam E.
Parker, Kevin Kit
Pourquié, Olivier
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_8285911
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_8285911
Other Identifiers
ISSN
0027-8424
E-ISSN
1091-6490
DOI
10.1073/pnas.2022960118
