Quantitative magnetic resonance imaging measures as biomarkers of disease progression in boys with D...
Quantitative magnetic resonance imaging measures as biomarkers of disease progression in boys with Duchenne muscular dystrophy: a phase 2 trial of domagrozumab
About this item
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Author / Creator
Sherlock, Sarah P. , Palmer, Jeffrey , Wagner, Kathryn R. , Abdel-Hamid, Hoda Z. , Bertini, Enrico , Tian, Cuixia , Mah, Jean K. , Kostera-Pruszczyk, Anna , Muntoni, Francesco , Guglieri, Michela , Brandsema, John F. , Mercuri, Eugenio , Butterfield, Russell J. , McDonald, Craig M. , Charnas, Lawrence and Marraffino, Shannon
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Journal title
Language
English
Formats
Publication information
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Subjects
More information
Scope and Contents
Contents
Duchenne muscular dystrophy (DMD) is a progressive, neuromuscular disorder caused by mutations in the
DMD
gene that results in a lack of functional dystrophin protein. Herein, we report the use of quantitative magnetic resonance imaging (MRI) measures as biomarkers in the context of a multicenter phase 2, randomized, placebo-controlled clinic...
Alternative Titles
Full title
Quantitative magnetic resonance imaging measures as biomarkers of disease progression in boys with Duchenne muscular dystrophy: a phase 2 trial of domagrozumab
Authors, Artists and Contributors
Author / Creator
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_9294028
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_9294028
Other Identifiers
ISSN
0340-5354,1432-1459
E-ISSN
1432-1459
DOI
10.1007/s00415-022-11084-0
