Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics an...
Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics and characteristics from the STRIDE Registry
About this item
Full title
Author / Creator
Muntoni, Francesco , Desguerre, Isabelle , Guglieri, Michela , Osorio, Andrés Nascimento , Kirschner, Janbernd , Tulinius, Már , Buccella, Filippo , Elfring, Gary , Werner, Christian , Schilling, Traci , Trifillis, Panayiota , Zhang, Olivia , Delage, Abdallah , Santos, Claudio L and Mercuri, Eugenio
Publisher
England: Future Medicine Ltd
Journal title
Language
English
Formats
Publication information
Publisher
England: Future Medicine Ltd
Subjects
More information
Scope and Contents
Contents
Strategic Targeting of Registries and International Database of Excellence (STRIDE) is an ongoing, multicenter registry providing real-world evidence regarding ataluren use in patients with nonsense mutation Duchenne muscular dystrophy (DMD) in clinical practice (NCT02369731). Here, we describe the initial demographic characteristics of the registr...
Alternative Titles
Full title
Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics and characteristics from the STRIDE Registry
Authors, Artists and Contributors
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_swepub_primary_oai_gup_ub_gu_se_287625
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_swepub_primary_oai_gup_ub_gu_se_287625
Other Identifiers
ISSN
2042-6305
E-ISSN
2042-6313
DOI
10.2217/cer-2019-0086
