Development of new outcome measures for adult SMA type III and IV: a multimodal longitudinal study
Development of new outcome measures for adult SMA type III and IV: a multimodal longitudinal study
About this item
Full title
Author / Creator
Querin, Giorgia , Lenglet, Timothée , Debs, Rabab , Stojkovic, Tanya , Behin, Anthony , Salachas, François , Le Forestier, Nadine , Amador, Maria Del Mar , Bruneteau, Gaëlle , Laforêt, Pascal , Blancho, Sophie , Marchand-Pauvert, Véronique , Bede, Peter , Hogrel, Jean-Yves and Pradat, Pierre-François
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Journal title
Language
English
Formats
Publication information
Publisher
Berlin/Heidelberg: Springer Berlin Heidelberg
Subjects
More information
Scope and Contents
Contents
Objective
The aim of this study was the comprehensive characterisation of longitudinal clinical, electrophysiological and neuroimaging measures in type III and IV adult spinal muscular atrophy (SMA) with a view to propose objective monitoring markers for future clinical trials.
Methods
Fourteen type III or IV SMA patients underwent standar...
Alternative Titles
Full title
Development of new outcome measures for adult SMA type III and IV: a multimodal longitudinal study
Authors, Artists and Contributors
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_hal_primary_oai_HAL_hal_03230903v1
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_hal_primary_oai_HAL_hal_03230903v1
Other Identifiers
ISSN
0340-5354
E-ISSN
1432-1459
DOI
10.1007/s00415-020-10332-5
