A new drug for rare diseases: pozelimab for CHAPLE disease
A new drug for rare diseases: pozelimab for CHAPLE disease
About this item
Full title
Author / Creator
Publisher
England: Elsevier Ltd
Journal title
Language
English
Formats
Publication information
Publisher
England: Elsevier Ltd
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More information
Scope and Contents
Contents
Unfortunately, many rare diseases still do not have therapeutic options, making them so-called orphan diseases. [...]collaboration between the pharmaceutical industry and the academic community is essential to develop new therapies for rare diseases. The low numbers of patients often make randomised controlled trials in rare diseases unfeasible. [....
Alternative Titles
Full title
A new drug for rare diseases: pozelimab for CHAPLE disease
Authors, Artists and Contributors
Author / Creator
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Primary Identifiers
Record Identifier
TN_cdi_hal_primary_oai_HAL_hal_04888413v1
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_hal_primary_oai_HAL_hal_04888413v1
Other Identifiers
ISSN
0140-6736,1474-547X
E-ISSN
1474-547X
DOI
10.1016/S0140-6736(23)02652-1
