Sustained Benefit from ivacaftor demonstrated by combining clinical trial and cystic fibrosis patien...
Sustained Benefit from ivacaftor demonstrated by combining clinical trial and cystic fibrosis patient registry data
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Full title
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Publisher
United States: American Thoracic Society
Journal title
Language
English
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Publication information
Publisher
United States: American Thoracic Society
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Scope and Contents
Contents
In clinical trials, patients with cystic fibrosis and a G551D mutation who received ivacaftor experienced improvements in pulmonary and nutritional outcomes. However, whether these improvements reflect a change in disease trajectory cannot be determined without longer-term analyses with an appropriate comparator population.
To examine, over a 3-...
Alternative Titles
Full title
Sustained Benefit from ivacaftor demonstrated by combining clinical trial and cystic fibrosis patient registry data
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Record Identifier
TN_cdi_proquest_miscellaneous_1718904372
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_1718904372
Other Identifiers
ISSN
1073-449X
E-ISSN
1535-4970
DOI
10.1164/rccm.201503-0578OC
