Gene therapy using haematopoietic stem and progenitor cells
Gene therapy using haematopoietic stem and progenitor cells
About this item
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Publisher
London: Nature Publishing Group UK
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Language
English
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Publisher
London: Nature Publishing Group UK
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Scope and Contents
Contents
Haematopoietic stem and progenitor cell (HSPC) gene therapy has emerged as an effective treatment modality for monogenic disorders of the blood system such as primary immunodeficiencies and β-thalassaemia. Medicinal products based on autologous HSPCs corrected using lentiviral and gammaretroviral vectors have now been approved for clinical use, and...
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Full title
Gene therapy using haematopoietic stem and progenitor cells
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TN_cdi_proquest_miscellaneous_2483406445
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_proquest_miscellaneous_2483406445
Other Identifiers
ISSN
1471-0056
E-ISSN
1471-0064
DOI
10.1038/s41576-020-00298-5
