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Development of Engineered-U1 snRNA Therapies: Current Status

Development of Engineered-U1 snRNA Therapies: Current Status

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_10572768

Development of Engineered-U1 snRNA Therapies: Current Status

About this item

Full title

Development of Engineered-U1 snRNA Therapies: Current Status

Publisher

Basel: MDPI AG

Journal title

International journal of molecular sciences, 2023-09, Vol.24 (19), p.14617

Language

English

Formats

Publication information

Publisher

Basel: MDPI AG

More information

Scope and Contents

Contents

Splicing of pre-mRNA is a crucial regulatory stage in the pathway of gene expression. The majority of human genes that encode proteins undergo alternative pre-mRNA splicing and mutations that affect splicing are more prevalent than previously thought. Targeting aberrant RNA(s) may thus provide an opportunity to correct faulty splicing and potential...

Alternative Titles

Full title

Development of Engineered-U1 snRNA Therapies: Current Status

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_10572768

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_10572768

Other Identifiers

ISSN

1422-0067,1661-6596

E-ISSN

1422-0067

DOI

10.3390/ijms241914617

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