Head-to-head trial of pegunigalsidase alfa versus agalsidase beta in patients with Fabry disease and...
Head-to-head trial of pegunigalsidase alfa versus agalsidase beta in patients with Fabry disease and deteriorating renal function: results from the 2-year randomised phase III BALANCE study
About this item
Full title
Author / Creator
Wallace, Eric L , Goker-Alpan, Ozlem , Wilcox, William R , Holida, Myrl , Bernat, John , Longo, Nicola , Linhart, Aleš , Hughes, Derralynn A , Hopkin, Robert J , Tøndel, Camilla , Langeveld, Mirjam , Giraldo, Pilar , Pisani, Antonio , Germain, Dominique Paul , Mehta, Ankit , Deegan, Patrick B , Molnar, Maria Judit , Ortiz, Damara , Jovanovic, Ana , Muriello, Michael , Barshop, Bruce A , Kimonis, Virginia , Vujkovac, Bojan , Nowak, Albina , Geberhiwot, Tarekegn , Kantola, Ilkka , Knoll, Jasmine , Waldek, Stephen , Nedd, Khan , Karaa, Amel , Brill-Almon, Einat , Alon, Sari , Chertkoff, Raul , Rocco, Rossana , Sakov, Anat and Warnock, David G
Publisher
England: BMJ Publishing Group Ltd
Journal title
Language
English
Formats
Publication information
Publisher
England: BMJ Publishing Group Ltd
Subjects
More information
Scope and Contents
Contents
BackgroundPegunigalsidase alfa is a PEGylated α-galactosidase A enzyme replacement therapy. BALANCE (NCT02795676) assessed non-inferiority of pegunigalsidase alfa versus agalsidase beta in adults with Fabry disease with an annualised estimated glomerular filtration rate (eGFR) slope more negative than −2 mL/min/1.73 m2/year who had received agalsid...
Alternative Titles
Full title
Head-to-head trial of pegunigalsidase alfa versus agalsidase beta in patients with Fabry disease and deteriorating renal function: results from the 2-year randomised phase III BALANCE study
Authors, Artists and Contributors
Author / Creator
Goker-Alpan, Ozlem
Wilcox, William R
Holida, Myrl
Bernat, John
Longo, Nicola
Linhart, Aleš
Hughes, Derralynn A
Hopkin, Robert J
Tøndel, Camilla
Langeveld, Mirjam
Giraldo, Pilar
Pisani, Antonio
Germain, Dominique Paul
Mehta, Ankit
Deegan, Patrick B
Molnar, Maria Judit
Ortiz, Damara
Jovanovic, Ana
Muriello, Michael
Barshop, Bruce A
Kimonis, Virginia
Vujkovac, Bojan
Nowak, Albina
Geberhiwot, Tarekegn
Kantola, Ilkka
Knoll, Jasmine
Waldek, Stephen
Nedd, Khan
Karaa, Amel
Brill-Almon, Einat
Alon, Sari
Chertkoff, Raul
Rocco, Rossana
Sakov, Anat
Warnock, David G
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_11137442
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_11137442
Other Identifiers
ISSN
0022-2593,1468-6244
E-ISSN
1468-6244
DOI
10.1136/jmg-2023-109445
