Defining SOD1 ALS natural history to guide therapeutic clinical trial design
Defining SOD1 ALS natural history to guide therapeutic clinical trial design
About this item
Full title
Author / Creator
Bali, Taha , Self, Wade , Liu, Jingxia , Siddique, Teepu , Wang, Leo H , Bird, Thomas D , Ratti, Elena , Atassi, Nazem , Boylan, Kevin B , Glass, Jonathan D , Maragakis, Nicholas J , Caress, James B , McCluskey, Leo F , Appel, Stanley H , Wymer, James P , Gibson, Summer , Zinman, Lorne , Mozaffar, Tahseen , Callaghan, Brian , McVey, April L , Jockel-Balsarotti, Jennifer , Allred, Peggy , Fisher, Elena R , Lopate, Glenn , Pestronk, Alan , Cudkowicz, Merit E and Miller, Timothy M
Publisher
England: BMJ Publishing Group LTD
Journal title
Language
English
Formats
Publication information
Publisher
England: BMJ Publishing Group LTD
Subjects
More information
Scope and Contents
Contents
ImportanceUnderstanding the natural history of familial amyotrophic lateral sclerosis (ALS) caused by SOD1 mutations (ALSSOD1) will provide key information for optimising clinical trials in this patient population.ObjectiveTo establish an updated natural history of ALSSOD1.Design, setting and participantsRetrospective cohort study from 15 medical c...
Alternative Titles
Full title
Defining SOD1 ALS natural history to guide therapeutic clinical trial design
Authors, Artists and Contributors
Author / Creator
Self, Wade
Liu, Jingxia
Siddique, Teepu
Wang, Leo H
Bird, Thomas D
Ratti, Elena
Atassi, Nazem
Boylan, Kevin B
Glass, Jonathan D
Maragakis, Nicholas J
Caress, James B
McCluskey, Leo F
Appel, Stanley H
Wymer, James P
Gibson, Summer
Zinman, Lorne
Mozaffar, Tahseen
Callaghan, Brian
McVey, April L
Jockel-Balsarotti, Jennifer
Allred, Peggy
Fisher, Elena R
Lopate, Glenn
Pestronk, Alan
Cudkowicz, Merit E
Miller, Timothy M
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_5136332
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_5136332
Other Identifiers
ISSN
0022-3050
E-ISSN
1468-330X
DOI
10.1136/jnnp-2016-313521
