Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
About this item
Full title
Author / Creator
CHERISH Study Group , Mercuri, Eugenio , Darras, Basil T , Chiriboga, Claudia A , Day, John W , Campbell, Craig , Connolly, Anne M , Iannaccone, Susan T , Kirschner, Janbernd , Kuntz, Nancy L , Saito, Kayoko , Shieh, Perry B , Tulinius, Már , Mazzone, Elena S , Montes, Jacqueline , Bishop, Kathie M , Yang, Qingqing , Foster, Richard , Gheuens, Sarah , Bennett, C. Frank , Farwell, Wildon , Schneider, Eugene , De Vivo, Darryl C and Finkel, Richard S
Publisher
United States: Massachusetts Medical Society
Journal title
Language
English
Formats
Publication information
Publisher
United States: Massachusetts Medical Society
Subjects
More information
Scope and Contents
Contents
In this phase 3 trial, among children with later-onset spinal muscular atrophy, those who received nusinersen had improvement in motor-function scores and those who underwent a sham procedure did not.
Alternative Titles
Full title
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
Authors, Artists and Contributors
Author / Creator
Mercuri, Eugenio
Darras, Basil T
Chiriboga, Claudia A
Day, John W
Campbell, Craig
Connolly, Anne M
Iannaccone, Susan T
Kirschner, Janbernd
Kuntz, Nancy L
Saito, Kayoko
Shieh, Perry B
Tulinius, Már
Mazzone, Elena S
Montes, Jacqueline
Bishop, Kathie M
Yang, Qingqing
Foster, Richard
Gheuens, Sarah
Bennett, C. Frank
Farwell, Wildon
Schneider, Eugene
De Vivo, Darryl C
Finkel, Richard S
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_swepub_primary_oai_gup_ub_gu_se_265106
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_swepub_primary_oai_gup_ub_gu_se_265106
Other Identifiers
ISSN
0028-4793,1533-4406
E-ISSN
1533-4406
DOI
10.1056/NEJMoa1710504
