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Lentiviral gene therapy for X-linked chronic granulomatous disease

Lentiviral gene therapy for X-linked chronic granulomatous disease

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7115833

Publication information

Publisher

New York: Nature Publishing Group US

More information

Scope and Contents

Contents

Chronic granulomatous disease (CGD) is a rare inherited disorder of phagocytic cells
1
,
2
. We report the initial results of nine severely affected X-linked CGD (X-CGD) patients who received ex vivo autologous CD34
+
hematopoietic stem and progenitor cell-based lentiviral gene therapy following myeloablative conditioning in first...

Alternative Titles

Full title

Lentiviral gene therapy for X-linked chronic granulomatous disease

Identifiers

Primary Identifiers

Record Identifier

TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7115833

Permalink

https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7115833

Other Identifiers

ISSN

1078-8956,1546-170X

E-ISSN

1546-170X,1744-7933

DOI

10.1038/s41591-019-0735-5

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