Lentiviral gene therapy for X-linked chronic granulomatous disease
Lentiviral gene therapy for X-linked chronic granulomatous disease
About this item
Full title
Author / Creator
Net4CGD consortium , the Net4CGD consortium , Kohn, Donald B. , Booth, Claire , Kang, Elizabeth M. , Pai, Sung-Yun , Shaw, Kit L. , Santilli, Giorgia , Armant, Myriam , Buckland, Karen F. , Choi, Uimook , De Ravin, Suk See , Dorsey, Morna J. , Kuo, Caroline Y. , Leon-Rico, Diego , Rivat, Christine , Izotova, Natalia , Gilmour, Kimberly , Snell, Katie , Dip, Jinhua Xu-Bayford , Darwish, Jinan , Morris, Emma C. , Terrazas, Dayna , Wang, Leo D. , Bauser, Christopher A. , Paprotka, Tobias , Kuhns, Douglas B. , Gregg, John , Raymond, Hayley E. , Everett, John K. , Honnet, Geraldine , Biasco, Luca , Newburger, Peter E. , Bushman, Frederic D. , Grez, Manuel , Gaspar, H. Bobby , Williams, David A. , Malech, Harry L. , Galy, Anne and Thrasher, Adrian J.
Publisher
New York: Nature Publishing Group US
Journal title
Language
English
Formats
Publication information
Publisher
New York: Nature Publishing Group US
Subjects
More information
Scope and Contents
Contents
Chronic granulomatous disease (CGD) is a rare inherited disorder of phagocytic cells
1
,
2
. We report the initial results of nine severely affected X-linked CGD (X-CGD) patients who received ex vivo autologous CD34
+
hematopoietic stem and progenitor cell-based lentiviral gene therapy following myeloablative conditioning in first...
Alternative Titles
Full title
Lentiviral gene therapy for X-linked chronic granulomatous disease
Authors, Artists and Contributors
Author / Creator
the Net4CGD consortium
Kohn, Donald B.
Booth, Claire
Kang, Elizabeth M.
Pai, Sung-Yun
Shaw, Kit L.
Santilli, Giorgia
Armant, Myriam
Buckland, Karen F.
Choi, Uimook
De Ravin, Suk See
Dorsey, Morna J.
Kuo, Caroline Y.
Leon-Rico, Diego
Rivat, Christine
Izotova, Natalia
Gilmour, Kimberly
Snell, Katie
Dip, Jinhua Xu-Bayford
Darwish, Jinan
Morris, Emma C.
Terrazas, Dayna
Wang, Leo D.
Bauser, Christopher A.
Paprotka, Tobias
Kuhns, Douglas B.
Gregg, John
Raymond, Hayley E.
Everett, John K.
Honnet, Geraldine
Biasco, Luca
Newburger, Peter E.
Bushman, Frederic D.
Grez, Manuel
Gaspar, H. Bobby
Williams, David A.
Malech, Harry L.
Galy, Anne
Thrasher, Adrian J.
Identifiers
Primary Identifiers
Record Identifier
TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7115833
Permalink
https://devfeature-collection.sl.nsw.gov.au/record/TN_cdi_pubmedcentral_primary_oai_pubmedcentral_nih_gov_7115833
Other Identifiers
ISSN
1078-8956,1546-170X
E-ISSN
1546-170X,1744-7933
DOI
10.1038/s41591-019-0735-5
